As newborn screening and rapid DNA sequencing become routine, we are poised to catch and treat inherited diseases at their ...

This first-in-human trial is testing a highly unconventional method: delivering fat-derived stem cells from the patient ...

Panelists discuss how the future of polycythemia vera (PV) management will be shaped by advancements in targeted therapies, ...

Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies the ...

The clinical trial tech companies Medidata and Medable are both taking to the floor of the American Society of Clinical ...

Neuroscientists can now make precise genetic tweaks to the neurons that are most affected by brain diseases such as Parkinson ...

AMT-130 has been granted the FDA's Regenerative Medicine Advance Therapy (RMAT) designation and Breakthrough Therapy designation, the first therapy for Huntington's disease to receive an RMAT ...

Greater numbers of circulating stem cells increase the efficacy of in vivo gene therapy techniques, potentially reducing the price tag of lifesaving treatments.

STEMCELL Technologies, Canada's largest biotechnology company, is pleased to announce the acquisition of Cellular Highways Ltd from TTP Group Ltd. Cellular Highways is a biotechnology company based ne ...

Hovanesian: There are a whole host of drugs that are pursuing complement inhibition, and then other classes of drugs as well that promise to address GA and it’s hard to tell which will be most ...

Malvern-based Ocugen has been granted rare pediatric disease designation by the Food and Drug Administration for its ...

Join, an innovator in retirement plan technology, announced today the introduction of CONNECT, a modular, open architecture solution that allows recordkeeper partners to easily access their choice of ...