Givinostat should be available to people with Duchenne muscular dystrophy through a type of compassionate use scheme.

ITF, IntraBio and Orchard are among the companies that have won FDA nods in the past year for Duchenne muscular dystrophy, ...

The Duchenne muscular dystrophy (DMD) landscape across the seven major markets (7MM) - the US, France, Germany, Italy, Spain, ...

Entrada Therapeutics is finally able to get its Duchenne muscular dystrophy candidate (DMD) back on track after the FDA ...

In the phase 1/2 INSPIRE DUCHENNE trial, interim data showed an average microdystrophin expression of 110% among participants ...

I'm fighting a fatal disease that took the life of my brother. I work in biotech and know there are medical advances that ...

Research and development (R&D) expenses: R&D expenses were $81.8 million and $58.8 million for the quarters ended December 31, 2024 and 2023, respectively. R&D expenses were $281.4 million and $210.8 ...

Several places in Bihar were jolted by a 5.5-magnitude earthquake that struck Nepal early on Friday, with tremors felt in ...

Less than half of patients had undergone bone monitoring, suggesting a need for better clinical guidance and management of ...

DMD Systems Recovery, LLC (DMD) proudly announces its recognition on the 2025 MO 100 Top Impact CEO Ranking for the third consecutive year, reinforcing its commitment to sustainable and responsible ...

Solid Biosciences has surged back into the Duchenne muscular dystrophy (DMD) gene therapy race. | Solid Biosciences has ...

Capricor Therapeutics filed a BLA for deramiocel, showing promising results in slowing cardiac dysfunction in DMD ...