The father of a nine-year-old girl with a rare disease likened to childhood dementia has called for health bosses to prolong ...

With thousands of rare diseases affecting millions of families worldwide, one Tampa Bay lawmaker is taking action to position Florida as a national leader in genetic medicine.

The site became known as the Dragulin villa cemetery, part of the Tragurium communal necropolis in the Roman city of Tragurium, researchers said in a study published March 1 in the Journal of ...

Gene Hackman’s nephew has spoken about funeral plans for the late star. The two-time Oscar winning actor, 95, died of heart ...

Years ago, a family member was diagnosed with an extremely rare cancer: Liposarcoma of the Spermatic Cord. Fewer than 200 ...

Last year, a series of essays profiling quintessential public servants made up our “Who Is Government?” project. The effort ...

Jaguar expects first results in Q2 2025 of proof-of-concept investigator-initiated trials of crofelemer for the rare diseases short bowel syndrome with intestinal failure and microvillus inclusion dis ...

As health care costs continue to rise and the burden of chronic disease grows, data-driven insights will be essential in ...

Genetics plays a crucial role in the manifestation and progression of over 6,800 rare diseases, including but not limited to, genetic disorders, rare ...

Senators told the Trump administration that Dr. Dave Weldon didn’t have the votes to be confirmed, though he had believed his ...

The White House has pulled the nomination of Dave Weldon as CDC director hours before he was set to appear for his ...

It’s been just six months since Zevra Therapeutics scored an FD | Niemann-Pick disease type C therapy Miplyffa became ...